The Circle of Kindness Foundation has started accepting applications for the purchase of Zolgensma, unregistered in Russia, for children with spinal muscular atrophy, RIA Novosti reports with reference to the press service of the Ministry of Health.
At the moment, medical documents are being collected and the exact need for the drug in the regions of the country is being clarified, as well as dosages and delivery times.
“Zolgensma will be provided to children under the age of two years who have the indications for it based on the decision of medical boards,” the statement says.
SMA leads to a gradual loss of motor functions, and the affected individuals lose the ability to move and have breathing difficulties. Two drugs for the treatment of the disease have been registered in Russia: nusinersen (Spinraza) and risdiplam.